The FDA’s Center for Drug Evaluation and Research (CDER) released the annual report, “Advancing Health Through Innovation:

New Drug Therapy Approvals”, outlining new drugs approved for the first time.

The FDA’s Center for Drug Evaluation and Research (CDER) released the annual report, “Advancing Health Through Innovation:

New Drug Therapy Approvals”, outlining new drugs approved for the first time.

Included in the report were numerous approvals for treatments targeted at combatting rare diseases like cystic fibrosis, tenosynovial giant cell tumor, and sickle cell disease. Additional approvals were given to assist patients with erythropoietic protoporphyria, neuromyelitis optica spectrum disorder, systemic sclerosis-associated interstitial lung disease, and Duchenne muscular dystrophy. Because so few patients suffer from these diseases, there are often scarce or no drugs available to treat the conditions.

Orphan Drugs in Third world countries:

Millions of people in Third World countries do not have access to the health care, drugs and vaccines available in developed countries. 10 million children less than 5 years old die each year of infectious diseases for which treatments exist in developing countries. 3 million children die each year because they have not been immunised. 150 million women would like to wait longer between two pregnancies or limit them, but they do not have access contraception. The spread of the AIDS epidemic only widens the health gap between poor countries and developed countries.